289th ENMC international workshop: assessing and managing emerging AAV related toxicities after gene therapy for neuromuscular disorders, 26 - 28 September 2025, Hoofddorp, The Netherlands

Neuromuscul Disord. 2026 Jul 28:107371. doi: 10.1016/j.nmd.2026.107371. Online ahead of print.ABSTRACTAdeno-associated virus (AAV) mediated gene therapies has emerged as a potentially transformative treatment approaches for neuromuscular disorders, with two FDA-approved products now in widespread cl

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Non-Oncology Biomarkers in Precision Medicine: A Narrative Review

Ther Innov Regul Sci. 2026 Aug 29. doi: 10.1007/s43441-026-01041-8. Online ahead of print.ABSTRACTPrecision medicine has revolutionized oncology by leveraging biomarkers for individualized therapy selection, early diagnosis, and real-time disease monitoring. However, the application of biomarkers in

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